The breakthrough: High Point native honored for her work in gene therapy

When Santa Claus brought 10-year-old Kathy High a junior chemistry set for Christmas more than 60 years ago, he never could’ve imagined what an incredible gift he was giving her. And ...

Re-engineered human cells boost gene-editing particle potency across multiple delivery systems

Gene editing has emerged as a powerful approach for targeting the genetic causes of disease, but getting the editing ...

Gene Cure For Inherited Deafness Effective, Long Lasting, Clinical Trial Finds

By Dennis Thompson HealthDay ReporterTHURSDAY, April 23, 2026 (HealthDay News) — A new gene therapy to treat inherited ...

Gene therapy targets untreatable cystic fibrosis mutation affecting about 10% of patients

Cystic fibrosis is among the most common, known and studied genetic diseases. It affects over 100,000 people worldwide and ...
Managed Healthcare Executive

Facing the practical problems of gene therapy | AMCP Annual 2026

Providers and payers certainly face some formidable challenges when it comes to gene therapy, but it pales in comparison to ...

Novartis Secures Positive EU Backing for SMA Gene Therapy Itvisma

Novartis (NYSE:NVS) said the European Medicines Agency’s Committee for Medicinal Products for Human Use has issued a ...
Pharmaceutical Technology

Regeneron cuts White House pricing deal, offers new gene therapy for free

This White House deal will see Regeneron offer all its new medicines at “MFN prices”, while providing Otarmeni for free to eligible patients.

Gene-screen strategy separates Parkinson's promoters from protectors, revealing new drug targets

A novel strategy that combines computational and experimental approaches has allowed researchers at Baylor College of ...